This report also provides a detailed analysis of the current mucopolysaccharidosis marketed drugs and late-stage pipeline ...

Jobsite Fan Market projected to reach USD 1.43 billion by 2035, driven by demand for workplace safety, energy efficiency, and smart ventilation solutions. ROCKVILLE, MD , MD, UNITED STATES, July 15, ...

The FDA cited manufacturing issues but did not flag problems with Ultragenyx’s data package for UX111, with the biotech ...

During the two decades that lapsed since “ironome” was coined for the ensemble of proteins associated with iron metabolism, a surge of iron-driven biological processes have been recognized as ...

Following our analysis of the options activities associated with Ultragenyx Pharmaceutical, we pivot to a closer look at the company's own performance. With a volume of 9,702,498, the price of RARE is ...

Sly syndrome, or Mucopolysaccharidosis Type VII (MPS VII), is a rare genetic disorder caused by a deficiency in the enzyme β-glucuronidase, leading to glycosaminoglycan accumulation in tissues and ...

Morquio Syndrome, or Mucopolysaccharidosis Type IV (MPS IV), is a rare genetic disorder causing glycosaminoglycans (GAGs) buildup due to enzyme deficiencies, leading to severe skeletal and organ ...